Funded Awards January 2020


PI Agency Title
Jonathan Cooper ForeBatten Foundation Defining Peripheral and Enteric Nervous System disease in Juvenile Batten Disease
Jonathan Cooper Abeona Neuropathologic Evaluation of the Efficacy of Intrathecal AAV9-Mediated Gene Therapy for Cln1 Disease
Jorge Di Paola NIH/R01 Genomics of Megakaryocyte and Platelet Biology
Andrea Granados CDTR Safety and efficacy of a low carbohydrate diet in children with type 1 diabetes
Jeffrey Magee SLCH Foundation Pedal the Cause – Purchase of FACS Aria Fusion SORP
Anthony Orvedahl NIH/K08 Role of Autophagy in Regulating Cytokine-Induced Macrophage Cell Death and Systemic Inflammatory Responses
Ahmed Said CDI/FR Said Faculty Scholar
Laura Schuettpelz CDI/II Regulation of Normal and Malignant B Cells by Tetraspanin CD53
Funded Awards
Funded Grants September 2021

PI Agency Title Megan Cooper NIH/ UG3/UH3/Baylor College of Medicine Safety and Efficacy of Itacitinib in treatment of JAK/STAT gain of function disorders Amjad Horani CDI Mechanisms of Primary Ciliary Dyskinesia Cynthia Ortinau Brain & Behavior Research Foundation Association of Parental Psychological Distress with Brain and Neurodevelopment in Congenital Heart …

Funded Awards
Funded Grants August 2021

PI Agency Title Fahd Ahmad NIH/CCHMC EMS for Children: Pediatric Emergency Care Applied Research Network (PECARN)  Jonathan Cooper NIH/R56 Characterizing and testing the efficacy of AAV-mediated gene therapy in a novel CRISPR/Cas9 generated sheepmodel of Cln1 disease. Jorge Di Paola NIH/R01/Ohio State University A Reversible Aptamer Based Therapeutic to Treat …

Funded Awards
Funded Grants July 2021

PI Agency Title Mohamed Abdelbaki EIF/The Hospital for Sick Children 3CI Study: Childhood Cancer Combination Immunotherapy. Phase 1b and Expansion Study of Nivolumab Combination Immunotherapy in Children, Adolescent and Young Adult (CAYA) Patients with Relapsed/Refractory Hypermutant Cancers Amy Armstrong Aflac Foundation/Children’s Healthcare of Atlanta A Maintenance Protocol of Sirolimus in …