Funded Awards – October 2018

Funded Awards
PI Agency Title
F. Sessions Cole NIH/U01 Washington University School of Medicine Undiagnosed D…
Jonathan Cooper NIH/R43/Collaborations Pharmaceuticals, Inc. Enzyme Replacement Therapy For Infantile Onset Neurona…
Brian DeBosch Longer Life Foundation Leveraging Adaptive Hepatic Glucose Fasting Responses …
Amit Mathur NIH/R01/University of Virginia Predictive Informatics Monitoring in the Neonatal Inte…
Peter Michelson CFF Improving Patient Adherence Through Patient Partnershi…
Funded Awards
Funded Grants September 2021

PI Agency Title Megan Cooper NIH/ UG3/UH3/Baylor College of Medicine Safety and Efficacy of Itacitinib in treatment of JAK/STAT gain of function disorders Amjad Horani CDI Mechanisms of Primary Ciliary Dyskinesia Cynthia Ortinau Brain & Behavior Research Foundation Association of Parental Psychological Distress with Brain and Neurodevelopment in Congenital Heart …

Funded Awards
Funded Grants August 2021

PI Agency Title Fahd Ahmad NIH/CCHMC EMS for Children: Pediatric Emergency Care Applied Research Network (PECARN)  Jonathan Cooper NIH/R56 Characterizing and testing the efficacy of AAV-mediated gene therapy in a novel CRISPR/Cas9 generated sheepmodel of Cln1 disease. Jorge Di Paola NIH/R01/Ohio State University A Reversible Aptamer Based Therapeutic to Treat …

Funded Awards
Funded Grants July 2021

PI Agency Title Mohamed Abdelbaki EIF/The Hospital for Sick Children 3CI Study: Childhood Cancer Combination Immunotherapy. Phase 1b and Expansion Study of Nivolumab Combination Immunotherapy in Children, Adolescent and Young Adult (CAYA) Patients with Relapsed/Refractory Hypermutant Cancers Amy Armstrong Aflac Foundation/Children’s Healthcare of Atlanta A Maintenance Protocol of Sirolimus in …