Funded Grants July 2021

Mohamed AbdelbakiEIF/The Hospital for Sick Children3CI Study: Childhood Cancer Combination Immunotherapy. Phase 1b and Expansion Study of Nivolumab Combination Immunotherapy in Children, Adolescent and Young Adult (CAYA) Patients with Relapsed/Refractory Hypermutant Cancers
Amy ArmstrongAflac Foundation/Children’s Healthcare of AtlantaA Maintenance Protocol of Sirolimus in Combination with Metronomic Chemotherapy in Children with High-Risk Solid Tumors
Paul HruzICTS/ STARIn Vivo Validation of a Novel GLUT8 Inhibitor for Treatment of Non-Alcoholic Fatty Liver Disease
Allison KingASH Research CollaborativeASH Clinical Trials Network Award
Caroline LeeMissouri Foundation for HealthHearts at Home: Caring for Pregnant Mothers and Babies with Cardiac Disease
Shalini ShenoyKatz Foundation/Children’s Hospital Los AngelesClinical Study for: Sickle Cell Transplant Evaluation of Long Term and Late Effects Registry-STELLAR
Shalini ShenoyNIH/U01/National Marrow Donor ProgramHematopoietic Cell Transplantation Using Treosulfan-Based Conditioning for the Treatment of Bone Marrow Failure Diseases BMT CTN Protocol #1904
Funded Awards
Funded Grants September 2021

PI Agency Title Megan Cooper NIH/ UG3/UH3/Baylor College of Medicine Safety and Efficacy of Itacitinib in treatment of JAK/STAT gain of function disorders Amjad Horani CDI Mechanisms of Primary Ciliary Dyskinesia Cynthia Ortinau Brain & Behavior Research Foundation Association of Parental Psychological Distress with Brain and Neurodevelopment in Congenital Heart …

Funded Awards
Funded Grants August 2021

PI Agency Title Fahd Ahmad NIH/CCHMC EMS for Children: Pediatric Emergency Care Applied Research Network (PECARN)  Jonathan Cooper NIH/R56 Characterizing and testing the efficacy of AAV-mediated gene therapy in a novel CRISPR/Cas9 generated sheepmodel of Cln1 disease. Jorge Di Paola NIH/R01/Ohio State University A Reversible Aptamer Based Therapeutic to Treat …

Funded Awards
Funded Grants June 2021

PI Agency Title Mohamed Abdelbaki SLCH Foundation Pediatric Neuro-Oncology Fellowship 2021-2022 Francis Cole NIH Admin Supplement: Washington University School of Medicine Undiagnosed Diseases Network Clinical Site Megan Cooper SLCH Foundation Center for Pediatric Immunology Patricia Dickson NIH/R21 Gene therapy with modified GlcNAc-1-phosphotransferase for mucolipidosis Patricia Dickson NIH/T32 Postdoctoral Training Program …