November 2019 Funded Awards

Funded Awards

 

PI Agency Title
Patricia Dickson NIH/ R61/R33 Recombinant Alpha-N-Acetylglucosaminidase with Improved Mannose 6-Phosphorylation for Treatment of Sanfilippo B Syndrome
Jane Garbutt SLCH Foundation WU PAARC Mental Health Care Collaborative
Misty Good Takeda Takeda Sponsored Research Agreement
Peter Michelson CFF/University of North Carolina at Chapel Hill Assessing Effectiveness of CF Infection Prevention & Control Guidelines
Stephen Pak Casma Casma Collaboration
Kimberly Quayle Medical College of Wisconsin/Medical College of Wisconsin Oral Penicillin Challenge in the Pediatric Emergency Department
Kristine Wylie The Medical Foundation at HRiA/Ann & Robert H. Lurie Children’s Hospital of Chicago A New Human Hepacivirus as an Etiologic Agent of Kawasaki Disease
Funded Awards
Funded Grants September 2021

PI Agency Title Megan Cooper NIH/ UG3/UH3/Baylor College of Medicine Safety and Efficacy of Itacitinib in treatment of JAK/STAT gain of function disorders Amjad Horani CDI Mechanisms of Primary Ciliary Dyskinesia Cynthia Ortinau Brain & Behavior Research Foundation Association of Parental Psychological Distress with Brain and Neurodevelopment in Congenital Heart …

Funded Awards
Funded Grants August 2021

PI Agency Title Fahd Ahmad NIH/CCHMC EMS for Children: Pediatric Emergency Care Applied Research Network (PECARN)  Jonathan Cooper NIH/R56 Characterizing and testing the efficacy of AAV-mediated gene therapy in a novel CRISPR/Cas9 generated sheepmodel of Cln1 disease. Jorge Di Paola NIH/R01/Ohio State University A Reversible Aptamer Based Therapeutic to Treat …

Funded Awards
Funded Grants July 2021

PI Agency Title Mohamed Abdelbaki EIF/The Hospital for Sick Children 3CI Study: Childhood Cancer Combination Immunotherapy. Phase 1b and Expansion Study of Nivolumab Combination Immunotherapy in Children, Adolescent and Young Adult (CAYA) Patients with Relapsed/Refractory Hypermutant Cancers Amy Armstrong Aflac Foundation/Children’s Healthcare of Atlanta A Maintenance Protocol of Sirolimus in …